See what the lab has been up to in the media

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Penn Med, Children’s Hospital of Philadelphia receive $14 million grant for gene-editing research

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New FDA Designations May Jumpstart Gene Therapy Development

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Children's Hospital of Philadelphia Researchers Report Encouraging First Evidence of Effective New Gene Therapy to Treat Multiple Sulfatase Deficiency

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Elucidating Shared Mechanisms of Pediatric and Adult Neurodegeneration

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